Congenital Anemias
Showing 1 - 25 of 1,816
Congenital Hemolytic Anemia, Sickle Cell Disease Trial run by the National Heart, Lung, and Blood Institute (NHLBI) (Peripheral
Recruiting
- Congenital Hemolytic Anemia
- Sickle Cell Disease
- Peripheral blood hematopoietic progenitor cell (PBPC) transplant
- +3 more
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Jan 25, 2023
Sickle Cell Anemia Trial run by the NHLBI (PBSC Transplant, Alemtuzumab, Sirolimus)
Active, not recruiting
- Sickle Cell Anemia
- PBSC Transplant
- +4 more
-
Bethesda, MarylandNational Institutes of Health Clinical Center, 9000 Rockville Pi
Oct 13, 2022
Sickle Cell Disease and Thalassemia Trial in Dallas (Donor Stem Cell Transplantation)
Withdrawn
- Sickle Cell Disease and Thalassemia
- Donor Stem Cell Transplantation
-
Dallas, TexasUT Southwestern Medical Center
Jul 22, 2021
Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
Recruiting
- Primary Immunodeficiency (PID)
- +4 more
- data collection
-
Pittsburgh, PennsylvaniaUPMC Children's Hospital of Pittsburgh
Feb 9, 2022
Parvovirus B19 Infection in Hereditary Hemolytic Anemias
Active, not recruiting
- Parvovirus B19 Infection
- Supportive treatment with or without red cell transfusion/intravenous immune globulin (IVIG)
-
Sohag, Egypt, Faculty of Medicine, Sohag University
Mar 25, 2021
Hemoglobinopathies and Rare Inherited Anemia and Covid 19
Recruiting
- Haemoglobinopathies
-
Genova, Italy
- +1 more
May 4, 2022
Sickle Cell Disease Trial run by the National Heart, Lung, and Blood Institute (NHLBI) (haploidentical stem cell transplant,
Recruiting
- Sickle Cell Disease
- haploidentical stem cell transplant
- +5 more
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Aug 18, 2022
Myeloid Chimerism Trial run by the National Heart, Lung, and Blood Institute (NHLBI) (CliniMACS CD34 Reagent)
Recruiting
- Myeloid Chimerism
- CliniMACS CD34 Reagent
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Apr 7, 2022
Pulmonary Hypertension (PAH) in Patients With Thalassemia
Completed
- Thalassemia Major
- +2 more
- Physician standard-of-care according to ESC/ERS Guidelines
-
Orbassano, Turin, Italy
- +7 more
Aug 3, 2022
Congenital Dyserythropoietic Anemia (CDA) Trial in Cincinnati
Recruiting
- Congenital Dyserythropoietic Anemia (CDA)
-
Cincinnati, OhioCincinnati Children's Hospital Medical Center
Feb 11, 2021
Congenital Heart Disease Trial in Boston (Use of prebypass ultrafiltration (PBUF))
Terminated
- Congenital Heart Disease
- Use of prebypass ultrafiltration (PBUF)
-
Boston, MassachusettsBoston Children's Hospital
Feb 14, 2022
Pattern of Congenital Hypothyroidism in Newborns.
Not yet recruiting
- Pattern of CH
- (no location specified)
Sep 26, 2023
Hematological Disorders Associated With COVID-19 Infection
Completed
- Hematological Condition With COVID19
-
Assiut, EgyptFacility of medicine
Jan 6, 2023
SGLT2 for Heart Failure in CHD Patients
Not yet recruiting
- Heart Failure
-
Nice, FranceUniversity hospital of Nice
Jun 7, 2023
Congenital Syphilis in Switzerland
Completed
- Congenital Syphilis
- Epidemiological study
-
Geneva, SwitzerlandLaurence Toutous Trellu
Jul 27, 2023
Neonatal Duodenal Atresia
Recruiting
- Congenital Duodenal Atresia
-
Strasbourg, FranceService de Chirurgie pédiatrique - CHU de Strasbourg - France
Oct 30, 2023
Heart Defects, Congenital, Cardiovascular Disease Other Trial in Columbus (Physical Activity Monitoring, Tailored Exercise
Recruiting
- Heart Defects, Congenital
- Cardiovascular Disease Other
- Physical Activity Monitoring
- +3 more
-
Columbus, OhioNationwide Children's Hospital
Aug 23, 2023
Pyeloplasty Trial (pyeloplasty)
Not yet recruiting
- Pyeloplasty
- pyeloplasty
- (no location specified)
Nov 20, 2023
Visual Prognosis and Complications of Ectopia Lentis Lens
Recruiting
- Ectopia Lentis
- Dislocation, Lens
-
Guangzhou, Guangdong, ChinaGuangdong Provincial Clinical Research Center for Ocular Disease
Dec 23, 2022
Closed-loop Management System of Congenital Talipes Equinovarus
Recruiting
- Prenatal Diagnosis and Closed-loop Management System of Congenital Talipes Equinovarus
-
Nanjing, Jiangsu, ChinaDrum Tower hospital
Nov 27, 2022
Frailty and Non-Fragile Congenital Heart Disease
Not yet recruiting
- Congenital Heart Disease
- Frailty
- Observational
- (no location specified)
Apr 10, 2023
Genetic Diagnosis in Congenital Cataracts
Completed
- Congenital Cataract
- Ophthalmic examination
- Whole-exome sequencing
-
Guangzhou, Guangdong, ChinaZhongshan Ophthalmic Center, Sun Yat-sen University
Mar 12, 2023
Congenital Heart Disease in Pregnancy, Prenatal Diagnosis, Fetal Echocardiography Trial (Improvement on Prenatal Screening and
Not yet recruiting
- Congenital Heart Disease in Pregnancy
- +2 more
- Improvement on Prenatal Screening and Treatment Capabilities for Congenital Heart Disease with a Comprehensive Diagnosis and Treatment Program Incorporating New Technologies
- (no location specified)
Jul 2, 2023
To Evaluate the Scaling Clinical Study of AAV2-RPE65 Gene Therapy Agent (LX101) in Patients With Congenital Amaurosis (LCA)
Not yet recruiting
- To Evaluate the Scaling Clinical Study of AAV2-RPE65 Gene Therapy Agent (LX101) in Patients With Congenital Amaurosis (LCA)
- (no location specified)
Aug 29, 2023
Congenital Diaphragmatic Hernias Trial in Hartford (Fetoscopic Endoluminal Tracheal Occlusion (FETO))
Recruiting
- Congenital Diaphragmatic Hernias
- Fetoscopic Endoluminal Tracheal Occlusion (FETO)
-
Hartford, ConnecticutConnecticut Children's Medical Center
Sep 26, 2023