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Congenital Anemias

Showing 1 - 25 of 1,816

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Congenital Hemolytic Anemia, Sickle Cell Disease Trial run by the National Heart, Lung, and Blood Institute (NHLBI) (Peripheral

Recruiting
  • Congenital Hemolytic Anemia
  • Sickle Cell Disease
  • Peripheral blood hematopoietic progenitor cell (PBPC) transplant
  • +3 more
  • Bethesda, Maryland
    National Institutes of Health Clinical Center
Jan 25, 2023

Sickle Cell Anemia Trial run by the NHLBI (PBSC Transplant, Alemtuzumab, Sirolimus)

Active, not recruiting
  • Sickle Cell Anemia
  • PBSC Transplant
  • +4 more
  • Bethesda, Maryland
    National Institutes of Health Clinical Center, 9000 Rockville Pi
Oct 13, 2022

Sickle Cell Disease and Thalassemia Trial in Dallas (Donor Stem Cell Transplantation)

Withdrawn
  • Sickle Cell Disease and Thalassemia
  • Donor Stem Cell Transplantation
  • Dallas, Texas
    UT Southwestern Medical Center
Jul 22, 2021

Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

Recruiting
  • Primary Immunodeficiency (PID)
  • +4 more
  • data collection
  • Pittsburgh, Pennsylvania
    UPMC Children's Hospital of Pittsburgh
Feb 9, 2022

Parvovirus B19 Infection in Hereditary Hemolytic Anemias

Active, not recruiting
  • Parvovirus B19 Infection
  • Supportive treatment with or without red cell transfusion/intravenous immune globulin (IVIG)
  • Sohag, Egypt
    , Faculty of Medicine, Sohag University
Mar 25, 2021

Hemoglobinopathies and Rare Inherited Anemia and Covid 19

Recruiting
  • Haemoglobinopathies
    • Genova, Italy
    • +1 more
    May 4, 2022

    Sickle Cell Disease Trial run by the National Heart, Lung, and Blood Institute (NHLBI) (haploidentical stem cell transplant,

    Recruiting
    • Sickle Cell Disease
    • haploidentical stem cell transplant
    • +5 more
    • Bethesda, Maryland
      National Institutes of Health Clinical Center
    Aug 18, 2022

    Myeloid Chimerism Trial run by the National Heart, Lung, and Blood Institute (NHLBI) (CliniMACS CD34 Reagent)

    Recruiting
    • Myeloid Chimerism
    • CliniMACS CD34 Reagent
    • Bethesda, Maryland
      National Institutes of Health Clinical Center
    Apr 7, 2022

    Pulmonary Hypertension (PAH) in Patients With Thalassemia

    Completed
    • Thalassemia Major
    • +2 more
    • Physician standard-of-care according to ESC/ERS Guidelines
    • Orbassano, Turin, Italy
    • +7 more
    Aug 3, 2022

    Congenital Dyserythropoietic Anemia (CDA) Trial in Cincinnati

    Recruiting
    • Congenital Dyserythropoietic Anemia (CDA)
      • Cincinnati, Ohio
        Cincinnati Children's Hospital Medical Center
      Feb 11, 2021

      Congenital Heart Disease Trial in Boston (Use of prebypass ultrafiltration (PBUF))

      Terminated
      • Congenital Heart Disease
      • Use of prebypass ultrafiltration (PBUF)
      • Boston, Massachusetts
        Boston Children's Hospital
      Feb 14, 2022

      Pattern of Congenital Hypothyroidism in Newborns.

      Not yet recruiting
      • Pattern of CH
        • (no location specified)
        Sep 26, 2023

        Hematological Disorders Associated With COVID-19 Infection

        Completed
        • Hematological Condition With COVID19
          • Assiut, Egypt
            Facility of medicine
          Jan 6, 2023

          SGLT2 for Heart Failure in CHD Patients

          Not yet recruiting
          • Heart Failure
            • Nice, France
              University hospital of Nice
            Jun 7, 2023

            Congenital Syphilis in Switzerland

            Completed
            • Congenital Syphilis
            • Epidemiological study
            • Geneva, Switzerland
              Laurence Toutous Trellu
            Jul 27, 2023

            Neonatal Duodenal Atresia

            Recruiting
            • Congenital Duodenal Atresia
              • Strasbourg, France
                Service de Chirurgie pédiatrique - CHU de Strasbourg - France
              Oct 30, 2023

              Heart Defects, Congenital, Cardiovascular Disease Other Trial in Columbus (Physical Activity Monitoring, Tailored Exercise

              Recruiting
              • Heart Defects, Congenital
              • Cardiovascular Disease Other
              • Physical Activity Monitoring
              • +3 more
              • Columbus, Ohio
                Nationwide Children's Hospital
              Aug 23, 2023

              Pyeloplasty Trial (pyeloplasty)

              Not yet recruiting
              • Pyeloplasty
              • pyeloplasty
              • (no location specified)
              Nov 20, 2023

              Visual Prognosis and Complications of Ectopia Lentis Lens

              Recruiting
              • Ectopia Lentis
              • Dislocation, Lens
                • Guangzhou, Guangdong, China
                  Guangdong Provincial Clinical Research Center for Ocular Disease
                Dec 23, 2022

                Closed-loop Management System of Congenital Talipes Equinovarus

                Recruiting
                • Prenatal Diagnosis and Closed-loop Management System of Congenital Talipes Equinovarus
                  • Nanjing, Jiangsu, China
                    Drum Tower hospital
                  Nov 27, 2022

                  Frailty and Non-Fragile Congenital Heart Disease

                  Not yet recruiting
                  • Congenital Heart Disease
                  • Frailty
                  • Observational
                  • (no location specified)
                  Apr 10, 2023

                  Genetic Diagnosis in Congenital Cataracts

                  Completed
                  • Congenital Cataract
                  • Ophthalmic examination
                  • Whole-exome sequencing
                  • Guangzhou, Guangdong, China
                    Zhongshan Ophthalmic Center, Sun Yat-sen University
                  Mar 12, 2023

                  Congenital Heart Disease in Pregnancy, Prenatal Diagnosis, Fetal Echocardiography Trial (Improvement on Prenatal Screening and

                  Not yet recruiting
                  • Congenital Heart Disease in Pregnancy
                  • +2 more
                  • Improvement on Prenatal Screening and Treatment Capabilities for Congenital Heart Disease with a Comprehensive Diagnosis and Treatment Program Incorporating New Technologies
                  • (no location specified)
                  Jul 2, 2023

                  To Evaluate the Scaling Clinical Study of AAV2-RPE65 Gene Therapy Agent (LX101) in Patients With Congenital Amaurosis (LCA)

                  Not yet recruiting
                  • To Evaluate the Scaling Clinical Study of AAV2-RPE65 Gene Therapy Agent (LX101) in Patients With Congenital Amaurosis (LCA)
                  • (no location specified)
                  Aug 29, 2023

                  Congenital Diaphragmatic Hernias Trial in Hartford (Fetoscopic Endoluminal Tracheal Occlusion (FETO))

                  Recruiting
                  • Congenital Diaphragmatic Hernias
                  • Fetoscopic Endoluminal Tracheal Occlusion (FETO)
                  • Hartford, Connecticut
                    Connecticut Children's Medical Center
                  Sep 26, 2023